Chief Executive Officer, Ultragenyx
Appears in 1 story
Leading two gene therapy launches in 2026
People with Glycogen Storage Disease Type Ia can't safely go without food. Their bodies can't release stored sugar, so many eat raw cornstarch around the clock, including overnight, to keep blood sugar from crashing. On August 19, 2026, the FDA approved GENGLYCOS, the first treatment aimed at the genetic cause of the disease rather than its symptoms.
Updated Aug 20
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