Gene therapy company
Appears in 1 story · Last updated Oct 1, 2026
As of October 2026: Sponsor of AMT-130; BLA and MAA under review, four-year data reported September 29, 2026
uniQure reported four-year data from its Huntington's gene therapy trial on September 29. The results were mixed: the main composite measure showed 44% slower decline, short of statistical significance, while a functional-capacity measure showed 61% slower decline.
Updated Oct 1
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