Professor of Cell & Gene Therapy, UCL Great Ormond Street Institute
Appears in 1 story
Lead researcher on BE-CAR7 base-edited therapy
Gene therapy killed Jesse Gelsinger in 1999. His death triggered FDA shutdowns, lawsuits, and nearly ended the field. Fast forward to December 2025: British scientists published results showing that base-edited immune cells—a 'living drug'—achieved deep remissions in 82% of children with previously incurable T-cell leukemia. Three years after treatment, 64% remain disease-free. Some patients are off treatment entirely.
Updated Jan 9
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