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Appears in 1 story · Last updated Sep 13, 2026
As of September 2026: Holds ex-US rights to zilganersen
Jenny Pearson's daughter Elise had her first seizure at 16 months. A scan a year later showed white splotches on her frontal lobe, and a genetic test confirmed Alexander disease, a rare progressive neurological disorder that had no treatment.
Updated Sep 13
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